Visit https://www.asgct.org/education for more free resources on gene and cell therapy, including progress on a number of promising treatments already in development.
Lots of genetic diseases come down to a small change in a single gene, but how do you treat those diseases when the cells involved don’t have any DNA?
Hosted by: Hank Green
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Sources:
https://www.nature.com/articles/ng1092-93
https://www.fda.gov/newsevents/newsroom/pressannouncements/ucm589467.htm
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Images:
https://commons.wikimedia.org/wiki/File:1911_Sickle_Cells.jpg
https://commons.wikimedia.org/wiki/File:Sickle_Cell_Anemia.png
https://commons.wikimedia.org/wiki/File:Protein_HBB_PDB_1a00.png
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